Cell and Gene Therapy Collaborative News & Announcements

Children’s Hospital of Philadelphia is the lead study site for the development of a gene therapy for multiple sulfatase deficiency.

Learn about a novel disorder caused by rare genetic variants, the importance of global neonatal outcomes, and more, in this week’s edition of In the News.

This month’s Featured Research Trainee for Asian American and Pacific Islander Heritage Month is Huijie (Jade) Feng, PhD

The Master of Regulatory Affairs program is accepting applications for the Fall 2023 academic year.

Cassie Kline, MD, MAS, and Jessica Foster, MD, received a seed grant to study CAR T-cell and radiotherapy for diffuse midline gliomas.

Two scientists with unique skill sets are developing an alternative method for gene therapy delivery with support from a CGTC Seed Grant.

In this Q&A, Drs. Teachey and Diorio discuss their partnership and research of a novel CAR T-cell therapy for one of the most common pediatric cancers.

In this Q&A, hematologist Dr. Kwiatkowski discusses the Food and Drug Administration approval of beti-cel (Zynteglo®), a gene therapy for beta thalassemia.

Next-generation DNA sequencing can predict relapse of patients with acute lymphoblastic leukemia treated with (CAR) T-cell therapy.

CHOP researchers have developed a novel cancer therapy that targets proteins inside cancer cells that are essential for tumor growth.

The peptide-centric CAR T cells, or PC-CARS, target cancer drivers in tumor cells previously thought unreachable.

CHOP researchers presented preliminary data that CRISPR therapy for inherited blood disorders is safe and effective.