Research Clinical Trials | CHOP Research Institute

Discovery Together

Children’s Hospital of Philadelphia is a leading site in the U.S. for world-changing pediatric clinical studies. We have a robust portfolio of active clinical research working with diverse patient populations across a variety of study types and fields. Comprehensive administrative research support ensures researchers at all levels perform highly productive, cost-effective studies that prioritize the patient-family experience. With the help of patients and healthy control participants, we’re finding answers to common, complex conditions and the rarest pediatric diseases. Check out our Research Discovery Finder for more information.

  • CHOP Research Institute is one of the nation’s largest recipients of National Institutes of Health funding made available to pediatric hospitals.
  • Annually, CHOP Research Institute has between 2,500 and 2,600 investigator-initiated, industry- and federally-sponsored, and foundation-supported IRB active protocols.
  • CHOP developed the first two FDA-approved gene therapies. Currently, more than two dozen cell and gene therapy trials are enrolling patients at CHOP.

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Featured Studies

Cornerstone Blog
This treatment is a potential game changer for patients who have required regular red blood transfusions to manage their disease, an intense treatment burden that comes with its own risks. – Janet Kwiatkowski, MD, MSCE