Gene Editing | CHOP Research Institute

Gene Editing

Published on
Sep 1, 2023
This week’s news roundup features three studies, Doris Duke Award winners, and a commitment to the CHOP Parkway Run & Walk.
Published on
Jul 31, 2023
Researchers developed a proof-of-concept model for delivering gene editing tools to treat blood disorders, allowing for the modification of diseased blood cells directly within the body.
Published on
Feb 3, 2023
In this news roundup, we celebrate research tools new and old, from RNA sequencing to gene editing to the best tool of all: collaboration.
Published on
May 26, 2021
The 17th Research Institute Scientific Symposium, held virtually on May 20, highlighted advances in cell and gene therapy.

Individuals with beta thalassemia that is treated with regular transfusions, and who are between the ages of 18 and 40 years old, may be able to participate.

The Human Pluripotent Stem Cell Core provides services for the development of novel, human cell-based experimental models for elucidating the pathophysiology of genetic disorders.

Published on
Oct 21, 2019
Join us in congratulating cell and gene therapy experts Beverly Davidson, PhD, and Stephan Grupp, MD, PhD, newly elected to the National Academy of Medicine.
Published on
Apr 19, 2019
Whether they study helmets on the football field or hemophilia in a lab, our scientists at Children’s Hospital of Philadelphia Research Institute are always on the cutting-edge of their respective fields, as the latest roundup of research news shows.

Dr. French came to CHOP in 2008 to establish the Human Pluripotent Stem Cell Core in the Center for Cellular and Molecular Therapeutics. She is an internationally recognized researcher involved in multi-investigator teams that utilize pluripotent stem cells for modeling human disease to study mechanism, development, and establish new therapeutic modalities.

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Published on
Nov 9, 2018
A landmark study provides proof-of-concept for prenatal gene editing to potentially prevent congenital disease.