Gene Editing | CHOP Research Institute
 

Gene Editing

In the News: RNA Sequencing, Neighborhood Opportunity, Doris Duke Award, Parkway Run & Walk, Gene Editing

Published on
Sep 1, 2023
in Cornerstone Blog
In the News: RNA Sequencing, Doris Duke Awards, Parkway Run & Walk
This week’s news roundup features three studies, Doris Duke Award winners, and a commitment to the CHOP Parkway Run & Walk.

‘Medicine of the Future’: Delivering mRNA Gene Editing Tools In Vivo

Published on
Jul 31, 2023
in Cornerstone Blog
‘Medicine of the Future’ in Development at CHOP to Treat Blood Disorders
Researchers developed a proof-of-concept model for delivering gene editing tools to treat blood disorders, allowing for the modification of diseased blood cells directly within the body.

In the News: Community-Driven Research, CRISPR, RNA Sequencing, Cover of the Year

Published on
Feb 3, 2023
in Cornerstone Blog
In the News
In this news roundup, we celebrate research tools new and old, from RNA sequencing to gene editing to the best tool of all: collaboration.

Scientific Symposium Gets to ‘Heart of Disease’ With Cell and Gene Therapy Talks

Published on
May 26, 2021
in Cornerstone Blog
17th Scientific Symposium Gets to ‘Heart of Disease’
The 17th Research Institute Scientific Symposium, held virtually on May 20, highlighted advances in cell and gene therapy.

Sangamo Gene Therapy for Thalassemia (ST-400-01)

Individuals with beta thalassemia that is treated with regular transfusions, and who are between the ages of 18 and 40 years old, may be able to participate.

Human Pluripotent Stem Cell Core

Human Pluripotent Stem Cell Core

The Human Pluripotent Stem Cell Core provides services for the development of novel, human cell-based experimental models for elucidating the pathophysiology of genetic disorders.

CHOP Cell and Gene Therapy Experts Elected to National Academy of Medicine

Published on
Oct 21, 2019
in Cornerstone Blog
Stephen A. Grupp and Beverly Davidson
Join us in congratulating cell and gene therapy experts Beverly Davidson, PhD, and Stephan Grupp, MD, PhD, newly elected to the National Academy of Medicine.

In the News: PAS 2019, NFL Helmet Safety, American Society of Gene and Cell Therapy, Bypass Prophylaxis Hemophilia, Lung Disease In Utero

Published on
Apr 19, 2019
in Cornerstone Blog
CHOP Research In the News
Whether they study helmets on the football field or hemophilia in a lab, our scientists at Children’s Hospital of Philadelphia Research Institute are always on the cutting-edge of their respective fields, as the latest roundup of research news shows.
Deborah L. French, PhD
Deborah French

Dr. French came to CHOP in 2008 to establish the Human Pluripotent Stem Cell Core in the Center for Cellular and Molecular Therapeutics. She is an internationally recognized researcher involved in multi-investigator teams that utilize pluripotent stem cells for modeling human disease to study mechanism, development, and establish new therapeutic modalities.

E-mail:
frenchd [at] chop.edu

Snapshot Science: How Can Gene Editing Breakthroughs Help Prevent Congenital Disease Before Birth?

Published on
Nov 9, 2018
in Cornerstone Blog
congenital disorders
A landmark study provides proof-of-concept for prenatal gene editing to potentially prevent congenital disease.