Dr. Pavani is the Director of the Human Pluripotent Stem Cell Core at Children’s Hospital of Philadelphia and a Research Assistant Professor in Pathology and Laboratory Medicine at the University of Pennsylvania.
Research news highlights a science breakthrough in CRISPR gene editing, and stem cell transplants provide curative potential for monogenic inflammatory bowel disease.
William Peranteau, MD, along with CHOP and Penn researchers are developing “one-and-done” new base-editing therapies for three genetic diseases of newborns.
Researchers developed a proof-of-concept model for delivering gene editing tools to treat blood disorders, allowing for the modification of diseased blood cells directly within the body.
