Viral Vectors | CHOP Research Institute

Viral Vectors

Our team at the Congenital Hyperinsulinism Center at CHOP is working on a research study to determine whether an experimental gene therapy product, DTX401, is safe and effective in people with glycogen storage disease type Ia (GSDIa)

Published on
Nov 5, 2021
The Clinical Vector Core, an award-winning, state-of-the-art, multi-product GMP manufacturing facility, supports the growing field of gene therapy.
Published on
Jul 26, 2021
Children’s Hospital of Philadelphia scientists developed a tunable switch system to control levels of gene therapy expression.

Understanding, developing, and applying gene and related cell and nucleic acid therapies to find cures for debilitating disorders.

Published on
Nov 13, 2019
Beverly Davidson, PhD, director of the Center for Cellular and Molecular Therapeutics, is advancing work on a gene therapy for Alzheimer’s.
Published on
Nov 6, 2018
Meet two of the scientists behind the game-changing gene therapies created by the Research Institute's Clinical Vector Core.
Published on
Oct 8, 2018
An infographic and article look at the science behind gene therapy, challenges faced by the field, and the road ahead.