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Results for Dystonia

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Pedro Gonzalez-Alegre, MD, PhD
Dr. Gonzalez-Alegre’s long-range research goal is to advance the application of precision medicine in the neurology clinic. His research focus revolves around genetic disorders that affect the brain, spanning from the diagnosis of novel genetic disease in the clinic to the identification of novel molecular targets using disease models and the design of early-phase human clinical trials.

Dr. Gonzalez-Alegre's long-range research goal is to advance the application of precision medicine in the neurology clinic. His research focus revolves around genetic disorders that affect the brain, spanning from the diagnosis of novel genetic disease in the clinic to the identification of novel molecular targets using disease models and the design of early-phase human clinical trials.

E-mail:
gonzalezap [at] chop.edu
Benjamin C. Kennedy, MD
Benjamin C. Kennedy

Dr. Kennedy's current research focuses on epilepsy genetics and epilepsy surgery, including stereo-EEG, hemispherotomy, corpus callosotomy, and vagal nerve stimulation.

E-mail:
kennedybc [at] chop.edu

Scientists Explore Gene Silencing as Novel Approach to Dystonia

Published on
Apr 24, 2015
in Cornerstone Blog
Scientists at The Children’s Hospital of Philadelphia are comparing two molecular therapy techniques for Dystonia — RNA interference (RNAi) and antisense oligonucleotides (ASOs).

Gonzalez-Alegre Laboratory

Gonzalez-Alegre Lab

The Gonzalez-Alegre Lab studies inherited genetic diseases of the nervous system, such as dystonia, Huntington’s disease, and inherited ataxias.

Kennedy Laboratory

Kennedy Laboratory

Dr. Kennedy's research focuses on epilepsy genetics and epilepsy surgery, including stereo-EEG, hemispherotomy, corpus callosotomy, and vagal nerve stimulation.

Validated Instruments

Validated Instruments

Study instruments and tools must be provided at the time of protocol submission. This page provides a list of instruments the IRB recognizes as validated, which therefore do not have to be attached to a submission for IRB review.

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  • Raymond G. Perelman Center for Cellular and Molecular Therapeutics (2)
  • Department of Surgery (1)
  • Division of Neurosurgery (1)
  • Epilepsy NeuroGenetics Initiative (ENGIN) (1)
  • Institutional Review Board (1)

In this section

Filter By

  • Principal Investigator / Faculty (2)

Organizations

  • Raymond G. Perelman Center for Cellular and Molecular Therapeutics (2)
  • Department of Surgery (1)
  • Division of Neurosurgery (1)
  • Epilepsy NeuroGenetics Initiative (ENGIN) (1)
  • Institutional Review Board (1)
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