This week we're all about getting smart in our highlights of research news from The Children's Hospital of Philadelphia. Getting smart in the approach to tackling childhood cancer means identifying strategies that will make a decade's progress in half the time - which is exactly the focus of the national Cancer Moonshot.
The research team concluded that early detection and gene therapy may offer the best results among infants diagnosed with Canavan disease. Canavan disease is a rare inherited neurological disorder with devastating effect. The lack of a specific enzyme, called aspartoacylase, causes the body's central nervous system to break down. The disease is usually fatal before a child reaches the teenage years.