Results for Beta Thalassemia

See highlights of work by Children’s Hospital of Philadelphia researchers that is leading to novel findings.

This week’s In the News highlights research on mitochondrial disease, acute lymphoblastic leukemia, type 2 diabetes, and sleep apnea.

In this Q&A, hematologist Dr. Kwiatkowski discusses the Food and Drug Administration approval of beti-cel (Zynteglo®), a gene therapy for beta thalassemia.

Learn about novel findings from our Children’s Hospital of Philadelphia researchers.

CHOP was a leading study site in the clinical trials that led to the FDAs approval of this therapy for patients who require regular blood transfusions.

In our latest news roundup, new findings on fetal hemoglobin, continuous positive airway pressure, and more.

This week’s In the News features endocrinology research, news on gene therapy in blood disorders, CAR T-cell therapy, and more.

This week’s news roundup features discoveries related to COVID-19’s effect on adolescents, autism screening, telemedicine, and more.

In the Emerging Innovators in Collaborative Research Program, up-and-coming researchers highlight their work.