Comprehensive Bone Marrow Failure Center News & Announcements

Symposium highlights AAV gene therapy best practices for children, CHOP researchers develop novel nanopore platform, and more In the News

This week, CHOP announces two new Frontier Programs, and researchers define the origins of hematopoietic failure in Fanconi anemia.

Researchers found exposing cells to a small molecule drug improves cell fitness during hematopoietic stem cell transplants, which could improve ex vivo gene therapy.

CHOP researchers find exposing cells to a small molecule drug improves cell fitness during hematopoietic stem cell transplants, which could improve ex vivo gene therapy.

This week’s roundup features new partnerships, novel findings, and exciting approaches to diagnosing rare conditions.

Study finds two laboratory findings can distinguish the autoimmune pathogenesis of aplastic anemia from other inherited bone marrow disorders.

This week’s roundup features research reinforcing the need for better universal surveillance for developmental delays and increased access to early intervention. This and more In The News.

Peter Kurre, MD, seeks to determine to what extent defects in fetal blood forming cells accelerate the loss of bone marrow function in young patients.

From research to the real world: Meet the six scholars in our Entrepreneurial Science Scholars Program at CHOP.

Bone marrow failure syndromes are rare disorders in which the bone marrow does not produce enough blood cells, increasing the risk for life-threatening bleeding, anemia, and infections.