Pediatric Translational Research Workshop

Course Information

The next CHOP Translational Research Workshop will take place on September 29 � October 2, 2015. Participants will be required to take part in the entire duration of the program and to abide by all guidelines and policies of The Children's Hospital of Philadelphia. Each day will be rooted in a specific theme that will introduce participants to various areas in translational research.

For more information and general questions, please contact the CHOP Office of Postdoctoral Affairs at

2013 Workshop Information

Taking place on October 14 � 18, 2013, 21 scientists participated in CHOP�s inaugural Translational Research Workshop for Basic Scientists. View the agenda and day-to-day descriptions of the event below.

View the agenda for the 2013 Translational Research Workshop

Monday, October 14, 2013 - What is Translational Research?

Day one of the Translational Research Workshop will provide attendees with an overview of how translational research is conducted in a hospital setting. Discussions and presentations will focus on the T1 through T4 "stages" of translational research. Leaders and experts from The Children's Hospital of Philadelphia and beyond will draw from their own experiences to demonstrate how basic research findings can be translated to meaningful clinical outcomes. Topics to be discussed include advances in HIV vaccine development, the discovery and development of the rotavirus vaccine, and more. The day will be capped off with attendees' first clinical experience focused on pediatric inflammatory bowel disease, one of the most significant chronic diseases affecting children and adolescents.

Tuesday, October 15, 2013 - Foundations of Translational Research

Developing a successful and profitable translational research program is a multifaceted process. On day two of the workshop, participants will explore more deeply the fundamentals of translational research, from clinical trial development to the ethics and economics of pediatric research. Workshop presenters will tackle topics such as pediatric cancer drug development and investigational drug treatment of neuroblastoma. Attendees will also have the opportunity to observe patients with a physician-researcher at the Children's Hospital neurology clinic.

Wednesday, October 16, 2013 - Human Genetics and Gene Therapy

On Wednesday, workshop participants will be privy to exciting new translational research projects taking place within the broad spectrum of human genetics and gene therapy. Children's Hospital investigators will discuss the identification of genes that contribute to congenital disease using state-of-the-art methodologies, and the successful translation of a novel genetic therapy that produces significant, long term improvement in a form of hereditary blindness. Participants will also tour the Gene Therapy Diagnostic Lab at Children's Hospital, and attend a live Institutional Review Board (IRB) meeting.

Thursday, October 17, 2013 - Human Disease and Therapeutics

Day four of the workshop will include a presentation from special guest speaker, Stephen Spielberg, MD, PhD, Editor-in-Chief, Therapeutic Innovation and Regulatory Science, at The Official Journal of the Drug Information Association. Dr. Spielberg, former Deputy Commissioner at the US Food and Drug Administration (FDA), will provide attendees with a unique perspective of translational research from the lens of the FDA. The founders of Vascular Magnetics, Inc., developers of a technology invented at Children's Hospital, will also be on hand to discuss the practical aspects of setting up a biotech. The day will continue with presenters on hand to share their research stories across a variety of disciplines, including metabolic disease, mitochondrial medicine, and bone and mineral metabolism. Patient visits to the classroom will follow, including a patient with the extremely rare condition Fibrodysplasia ossificans progressiva (FOP), also known as Stone Man Syndrome.

Friday, October 18, 2013 - 21st Century Pediatric Medicine

The final day of the Translational Research Workshop will focus on cutting edge advancements in the areas of pediatric research and medicine. Participants will learn about innovative practices in the areas of fetal surgery and pediatric intensive care from renowned experts, followed by a visit to the CHOP Pediatric Intensive Care Unit. A special luncheon session, presented in association with the CHOP Center for Autism Research, will focus specifically on research and innovation related to the autism spectrum disorders