Canavan disease is a rare inherited neurological disorder with devastating effect. The lack of a specific enzyme, called aspartoacylase, causes the body’s central nervous system to break down. The disease is usually fatal before a child reaches the teenage years.
Tag Archive: Neurology
Permanent link to this article: http://www.research.chop.edu/blog/gene-therapy-shows-promise-for-helping-children-with-canavan-disease/