High is one of the world’s leading experts in gene therapy, which has long been a “next big thing” in medicine: Take a person with a devastating genetic disease and replace their nonfunctional gene with a normal one — a cure built right into your DNA.
Tag Archive: blindness
Jan 16 2014
Permanent link to this article: http://www.research.chop.edu/blog/repairing-dna-one-cell-at-a-time/
May 02 2013
A groundbreaking clinical trial of gene therapy for a form of congenital blindness, sponsored by The Children’s Hospital of Philadelphia in collaboration with Penn Medicine, was recently recognized with the Distinguished Clinical Research Achievement Award from the Clinical Research Forum, an organization of clinical research centers, industry, and volunteer groups.
Permanent link to this article: http://www.research.chop.edu/blog/chop-penn-gene-therapy-trial-for-blindness-honored/