Researchers in the Center for Cellular and Molecular Therapeutics (CCMT) at The Children’s Hospital of Philadelphia suggest that an intricate pathway crucial to the development of Huntington’s disease (HD) rests on a “biological teeter-totter” that when carefully balanced could help to control this devastating neurodegenerative disorder.
Category Archive: Center for Cellular and Molecular Therapeutics
Permanent link to this article: http://www.research.chop.edu/blog/researchers-lay-groundwork-novel-therapy-huntingtons-disease/
Apr 02 2014
Permanent link to this article: http://www.research.chop.edu/blog/prominent-gene-therapy-expert-joins-chop/
Jan 16 2014
Permanent link to this article: http://www.research.chop.edu/blog/repairing-dna-one-cell-at-a-time/
Dec 11 2013
For her pioneering hemophilia and gene therapy research, Children’s Hospital hematologist Katherine A. High, MD, director of the Center for Cellular and Molecular Therapeutics (CCMT), was recently honored with the 2013 E. Donnall Thomas Lecture and Prize at the American Society of Hematology (ASH) Annual Meeting.
Permanent link to this article: http://www.research.chop.edu/blog/chop-hematologist-gene-therapy-researcher-honored/
Jul 25 2013
Permanent link to this article: http://www.research.chop.edu/blog/childrens-hospital-researchers-develop-bioengineered-decoy-to-improve-gene-therapy/
May 02 2013
A groundbreaking clinical trial of gene therapy for a form of congenital blindness, sponsored by The Children’s Hospital of Philadelphia in collaboration with Penn Medicine, was recently recognized with the Distinguished Clinical Research Achievement Award from the Clinical Research Forum, an organization of clinical research centers, industry, and volunteer groups.
Permanent link to this article: http://www.research.chop.edu/blog/chop-penn-gene-therapy-trial-for-blindness-honored/